Phase 1/2a Trial Of Srp-9001 In Patients With Duchenne Muscular Dystrophy: 3-Year Safety And Functional OutcomesJ. Mendell,Z. Sahenk,K. Lehman, C. Nease,L. Lowes, N. Reash, M. Iammarino,L. Alfano, J. Vaiea,S. Lewis,K. Church,R. Shell,R. Potter,D. Griffin, E. Pozsgai,M. Hogan,L. Rodino-KlapacNEUROMUSCULAR DISORDERS(2021)引用 0|浏览5暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要