Gene Replacement Therapy For Symptomatic Spinal Muscular Atrophy Type 1: Final Results Of The Phase Iii Str1ve-Eu Study F. Muntoni,G. Baranello,R. Masson, O. Boespflug-Tanguy, C. Bruno,S. Corti,A. Daron,N. Deconinck,L. Servais,V. Straub, H. Ouyang, D. Chand, S. Tauscher-Wisniewski, N. Mendonca,A. Lavrov,E. MercuriEUROPEAN JOURNAL OF NEUROLOGY(2021)引用 3|浏览16暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要