Gene Replacement Therapy For Symptomatic Spinal Muscular Atrophy Type 1: Final Results Of The Phase Iii Str1ve-Eu Study

F. Muntoni,G. Baranello,R. Masson, O. Boespflug-Tanguy, C. Bruno,S. Corti,A. Daron,N. Deconinck,L. Servais,V. Straub, H. Ouyang, D. Chand, S. Tauscher-Wisniewski, N. Mendonca,A. Lavrov,E. Mercuri

EUROPEAN JOURNAL OF NEUROLOGY(2021)

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