Early Safety And Efficacy Results With A Single Dose Of Autologous Crispr-Cas9-Modified Cd34+Hematopoietic Stem And Progenitor Cells In Transfusion-Dependent Beta-Thalassemia And Sickle Cell DiseaseJosu De La Fuente,Haydar Frangoul,Yael Bobruff,Maria Domenica Cappellini,Selim Corbacioglu,Christine Marie Fernandez,Stephan Grupp,Rupert Handgretinger,Tony W. Ho,Suzan Imren,Antonis Kattamis,Julie Lekstrom-Himes,Franco Locatelli,Yimeng Lu,Markus Mapara, Sarah Mulcahey,Mariane De Montalembert,Damiano Rondelli,Niraj Shanbhag,Sujit Sheth,Sandeep Soni,Martin H. Steinberg, Michael Weinstein,John Wu,Donna WallBRITISH JOURNAL OF HAEMATOLOGY(2021)引用 0|浏览8暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要