Long-Term Hematopoietic Stem Cell Lentiviral Gene Therapy Corrects Neuromuscular Manifestations In Preclinical Study Of Pompe MiceNiek P. Van Til,Yildirim Dogan,Cecilia Barese,Zeenath Unnisa,Swaroopa Guda,Rena Schindler,John Yoon,Mary Jacobs,Abhishek Chiyyeadu,Daniella Pizzurro,Bianling Liu,Mirjam Trame,Tim Maiwald,Christine Oborski,Axel Schambach,Claudia Harper,Richard Pfeifer,Chris MasonMOLECULAR THERAPY(2021)引用 0|浏览5暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要