Aav1.Nt-3 Gene Therapy Improves Phenotype In Garsnmf249/+ Mice, A Charcot-Marie-Tooth Axonal Type 2d (Cmt2d) Model
JOURNAL OF THE PERIPHERAL NERVOUS SYSTEM(2020)
关键词
CMT2D, GarsNmf249, Gene Therapy, AAV1, Neurotrophin-3
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