Enhanced Transduction Lentivector Gene Therapy For Treatment Of Older Patients With X-Linked Severe Combined Immunodeficiency
Suk See De Ravin, Sandra Anaya O'Brien,Nana Kwatemaa,Narda Theobald,Siyuan Liu,Janet Lee,Lela Kardava,Taylor Liu,Frederick Goldman,Susan Moir,Jack Bleesing,Benedicte Neven,Jennifer Puck,Morton J. Cowan,Ewelina Mamcarz,Stephen Gottschalk,Michael M. Meagher,Luigi Notarangelo,Elizabeth Kang,Xiaolin Wu,Harry L. Malech BLOOD(2019)
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