Magnetic Resonance Imaging Is A Valuable Tool To Evaluate The Therapeutic Efficacy Of Burosumab In Children With X-Linked Hypophosphatemia

EUROPEAN JOURNAL OF ENDOCRINOLOGY(2021)

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摘要
Federico Di Rocco1,14,15, Severine Trabado5,16, Dominique Prie7,17, Carolina Di Somma3, Annamaria Colao3, Catherine Adamsbaum1,4,5, Anya Rothenbuhler1,10 and Agnes Linglart1,5,10 1AP-HP, Reference Center for Rare Disorders of the Calcium and Phosphate Metabolism, Filiere OSCAR, EndoRare, BOND ERN and Platform of Expertise for Rare Diseases Paris-Saclay, Bicetre Paris-Saclay Hospital, Le Kremlin-Bicetre, France, 2Genethon, Paris-Saclay University, Univ Evry, Inserm, Integrare research unit UMR_S951, Evry, France, 3Division of Endocrinology, Department of Clinical Medicine and Surgery, University of Naples Federico II, Naples, Italy, 4AP-HP, Department of Pediatric Radiology, Bicetre Paris-Saclay Hospital, Le Kremlin-Bicetre, France, 5University Paris Saclay, Le Kremlin-Bicetre, France, 6AP-HP, Reference Center for Rare Disorders of the Calcium and Phosphate Metabolism, Dental Medicine Department, Bretonneau Hospital, GHN-Universite de Paris, Paris, France, 7Universite de Paris, Paris, France, 8Universite de Paris, Institut des maladies musculo-squelettiques, Laboratory Orofacial Pathologies, Imaging and Biotherapies URP2496 and FHU-DDS-Net, Dental School, and Plateforme d'Imagerie du Vivant (PIV), Montrouge, France,
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