PR001 gene therapy increased GCase activity and improved Gaucher disease type 1 phenotypes in mouse modelsPatty Sheehan,Laura D. Heckman,Li Chin Wong,Sid Kamalakaran, Zhaohui Yang,Hsuan-Ni Lin,Swetha Garimalla, Dominik Biezonski,Jeremiah Hendricks,Rekha Raghunathan, Zoe Zhao,Priyam Raut,Jason Politi,Yong Dai,Asa Abeliovich,Franz HeftiMOLECULAR THERAPY(2022)引用 0|浏览0暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要