First FDA-approved Human AAV Gene Therapy Clinical Trial in Adults with Early Manifest Huntington's Disease
Ralf Reilmann,Christopher Ross,Paul S. Larson,Michael D. Geschwind,Russell R. Lonser,William S. Anderson,Claudia M. Testa,Samuel A. Frank,Sandra K. Kostyk,Jee Bang,Melvin Evers,Martin de Haan, Astrid Valles-Sanchez, Kaity Renaud, Lori Enney, Patrick Yu,Alex Kuta, Scott McMilllan,Jacek Lubelski, Jaap Twisk,Pavlina Konstantinova,Sander van Deventer,Joseph J. Higgins NEUROTHERAPEUTICS(2019)
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