AAV.U7 technology for two mutational hotspots of the DMD gene (similar to 6%) results in efficient exon skipping, protein restoration and force improvementN. Wein,T. Simmons,D. Rajakumar, D. Lesman, D. Li, C. Gaffney, R. Rafferty, N. Huang,Y. Rodriguez,C. Young,M. Spencer, K. FlaniganNEUROMUSCULAR DISORDERS（2020）引用 0|浏览8暂无评分AI 理解论文溯源树样例生成溯源树，研究论文发展脉络Chat Paper正在生成论文摘要
