First-in-human intrathecal gene transfer study for giant axonal neuropathy: Three-year interim evaluation of safety and efficacyD. Bharucha-Goebel,D. Saade,M. Jain,G. Norato,D. Rybin,K. Cheung,M. Waite,E. Paredes,A. Foley,T. Lehky, Y. Hu, R. Calcedo Del Hoyo, J. Chichester, S. Jacobson,A. Nath,L. Charnas, R. Samulski, S. Gray,C. BonnemannNEUROMUSCULAR DISORDERS(2020)引用 0|浏览3暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要