Correction of GM2 Gangliosidosis in Neonatal, Juvenile, and Adult Sandhoff Mice Using a Bicistronic Hexosaminidase VectorKarlaina J. L. Osmon,Natalie Deschenes, Eminet Boagle,Shalini Kot,Zhilin Chen,Melissa Mitchell,Clifford Heindel, Jack G. Keimel,William F. Kaemmerer,Steven G. Gray,Jagdeep S. WaliaMOLECULAR THERAPY(2018)引用 0|浏览2暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要