Treatment of Methylmalonic Acidemia by Targeted Integration of MUT into Albumin Using an Optimized Promoterless AAV VectorLeah E. Venturoni,Randy J. Chandler,Nelson Chau,Jing Liao,Mark A. Kay,Adi Barzel,Charles P. VendittiMOLECULAR THERAPY(2019)引用 0|浏览4暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要