Optimizing Nuclease Specificity via Catalytic Domain Engineering Enables Complete Gene Modification with No Detectable Off-Targets

Edward J. Rebar,Deepak P. Patil, Charles B. Paine,Friedrich Fauser, Danny F. Xia, Nicholas A. Scarlott, Stephen C. Lam, Sarah J. Hinkley,David A. Shivak, Yuri R. Bendana,David E. Paschon,Lei Zhang,Gary Lee,Jeffrey C. Miller

MOLECULAR THERAPY(2019)

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