Oligodendrocyte Dysfunction and Global CNS Dysmyelination Occur in Arginase Deficiency That is Prevented with AAV-Based Hepatic Gene Therapy

Jenna Lambert,Xiao-Bo Liu,Suhail Khoja, Matt Nitzahn,Adam Eliav, Steve Cederbaum, Gerald S. Lipshutz

MOLECULAR THERAPY(2020)

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