Base Editing of Gamma Globin Gene Promoters Generates Durable Expression of Fetal Hemoglobin for the Treatment of Sickle Cell DiseaseAdrian P. Rybak, Elsie Zahr Akrawi,Conrad Rinaldi,Scott J. Haskett,Ling Lin,Jeffrey Marshall,Alexander Liquori,Luis Barrera,Jenny Olins,S. Haihua Chu,Jeremy Decker,Minerva Sanchez,Yeh-Chuin Poh, Matt Humes,Michael S. Packer,Nicole M. Gaudelli,Sarah Smith,Adam Hartigan,Giuseppe CiaramellaMOLECULAR THERAPY(2020)引用 2|浏览19AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要