Pathophysiological Mechanisms of Bone Defects and Impact of Ex Vivo Hematopoietic Stem Cell Gene Therapy in Mucopolysaccharidosis Type I HurlerLudovica Santi,Sara Penna,Stefania Crippa,Valentina Capo,Roberto Bosotti, Giulia Porro,Giada De Ponti,Francesca Tucci,Mara Riminucci,Alessandro Corsi,Marta Serafini,Bernhard Gentner,Alessandro Aiuti,Anna Villa,Maria Ester BernardoMOLECULAR THERAPY(2020)引用 0|浏览9暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要