Intravenous AAV Gene Therapy Improves Lifespan and Clinical Metrics in Feline Sandhoff DiseaseAnne S. Maguire,Elise B. Diffie,Amanda L. Gross, Hannah G. Lahey,Miguel Sena-Esteves,Douglas R. MartinMOLECULAR THERAPY(2020)引用 0|浏览15暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要