AAV Vector-Mediated Iduronidase Gene Delivery in a Murine Model of Mucopolysaccharidosis Type I: Comparing Different Routes of Delivery to the CNSLalitha Belur,Zhenhong Nan,Kelly M. Podetz-Pedersen,Carolyn A. Fairbanks,Leah R. Hanson,William H. Frey,Karen Kozarsky,Walter C. Low,R. Scott McIvorMOLECULAR THERAPY(2013)引用 0|浏览1暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要