Insertion of Short Double-Stranded Oligonucleotides Using CRISPR/Cas9 as a Therapeutic Approach for Glycogen Storage Disease Type 1aChristopher Hart,Kirsten Beaudry, TeQuana Bayless,Sarah J. Spencer,Nicholas Woodward, Muthusamy Jayaraman,John P. Leonard,Tony W. Ho, Troy CarloMOLECULAR THERAPY(2020)引用 1|浏览10暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要