Dual AAV Delivery of Otoferlin Durably Rescues Hearing in Congenitally Deaf Preclinical Models
Jonathon Whitton,Adam Palermo,Lars Becker,Joe Burns,Ning Pan,Martin Schwander,Xichun Zhang,Bifeng Pan, Lillian Smith,XuDong Wu,Arun Senapati, Elizabeth Amaro Gonzalez,Yong Ren,Tyler Gibson,Theresa Abel, Paul Liebesny,Fuxin Shi, Brad Enerson, Ren Nguyen, Noah Druckenbrod, Emma Alterman,Leah Sabin,Sarah Cancelarich,Meghan Drummond MOLECULAR THERAPY(2020)
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