Efficacy of Genz-682452-mediated inhibition of glucosylceramide synthase in a mouse model of Sandhoff diseaseJohn Marshall,Jennifer B. Nietupski,Dinesh Bangari,Hyejung Park, Kristen Randall,Drew Tietz,Bing Wang,Terry Wilper,John P. Leonard,Seng H. ChengMOLECULAR GENETICS AND METABOLISM(2018)引用 0|浏览18暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要