Integrated Safety Report for Intravenous (IV) Onasemnogene Abeparvovec Clinical Development Programs in Spinal Muscular Atrophy (SMA) Type 1 (SMA1)

S. Tauscher-Wisniewski,R. S. Finkel,E. Mercuri,R. Masson,J. Parsons, F. Baldinetti,D. Chand, A. Kleyn,D. M. Sproule, D. E. Feltner, J. R. Mendell

EUROPEAN JOURNAL OF NEUROLOGY(2020)

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