Haematopoietic stem cell gene editing for safe and effective correction of SCID-X1 G. Schiroli,S. Ferrari,A. Conway,V. Capo,A. Jacob,L. Albano,T. Plati,M. C. Castiello,F. Sanvito,C. Bovolenta,R. Palchaudhuri,D. T. Scadden,M. C. Holmes,A. Villa,G. Sitia,A. Lombardo,P. Genovese,L. NaldiniHUMAN GENE THERAPY(2017)引用 0|浏览31暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要