Bb-301: A Single Silence And Replace Aav-Based Vector For The Treatment Of Oculopharyngeal Muscular Dystrophy
HUMAN GENE THERAPY（2018）
关键词
oculopharyngeal muscular dystrophy,OPMD,gene therapy,AAV,silence and replace,PABPN1,siRNA
AI 理解论文
溯源树
样例
生成溯源树，研究论文发展脉络
Chat Paper
正在生成论文摘要