Homology-independent targeted integration to counteract toxic gain-of-functions and loss of transgene expression due to cell proliferation

M. Llado, F. Esposito,C. Iodice, R. Minopoli, H. Lyubenova, E. Nusco,A. Manfredi,M. Mutarelli, L. Di Filippo,V. Nigro,D. Cacchiarelli, A. Auricchio

HUMAN GENE THERAPY(2019)

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