Preliminary data from the first hematopoietic stem cell gene therapy trial with lentiviral vector demonstrate expression of the therapeutic protein in high percentage of lymphocytes and monocytes in two patients with X-linked adrenoleukodystrophyNathalie Cartier,Salima Hacein-Bey-Abina,Gabor Veres,Michel Vidaud,Liliane Dal-Cortivo,Laure Caccavelli,Nizar Malhaoui,Veronique Kiermer,Denice Mittelstaedt,Andrew Simmons,Celine Bellesme, Francoise Audat,Stephane Blanche, Pierre Charnaud,Muriel Audit, Bruno L'homme, Jing-Chao Zhao-Emmonet,Serge Fichelson,Francoise Pflumio, Anne Dubart-Kupperschmitt,Rachel Salzman,Amber Salzman,Pierre Bougneres,Alain Fischer, Marina Cavazzana-Calvo,Patrick AubourgHUMAN GENE THERAPY（2007）引用 0|浏览13暂无评分AI 理解论文溯源树样例生成溯源树，研究论文发展脉络Chat Paper正在生成论文摘要
