Advanced therapies for the treatment of erythroid metabolic diseases: The pyruvate kinase deficiency

M. Garcia-Gomez, Z. Garate,S. Navarro, O. Quintana-Bustamante, A. Krane, L. Cerrato,M. A. Martin,I. Orman,M. Garcia-Bravo, R. Sanchez-Dominguez,J. Sevilla,T. M. Maia,L. M. Ribeiro,N. Fusaki,F. Garcia-Sanchez, X. Aguirre,A. Gouble,F. Prosper,M. Antoniou,J. A. Bueren, B. R. Davis,J. Carlos Segovia

HUMAN GENE THERAPY(2013)

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