Gene knock-in using specific TALE nucleases restores erythroid differentiation defect of human iPSC obtained from pyruvate kinase deficient patients Z. Garate, O. Quintana-Bustamante, A. M. Crane, L. Cerrato,I. Orman,J. Sevilla,T. M. Maia,L. M. Ribeiro,N. Fusaki,F. Garcia-Sanchez, X. Aguirre,A. Gouble,F. Prosper,J. A. Bueren,B. R. Davis,J. Carlos SegoviaHUMAN GENE THERAPY(2013)引用 0|浏览14暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要