AXO-AAV-GM1 for the treatment of GM1 gangliosidosis: Program Overview G. Corcoran,P. Korner, J. Benoit,C. J. Tifft, H. Gray-Edwards, M. Sena-Esteves,D. R. MartinHUMAN GENE THERAPY(2019)引用 0|浏览13暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要