AAV-mediated gene editing as a potential therapeutic approach for C9ORF72-linked ALS/FTD J. Alves-Cruzeiro,E. Karyka,C. Bauer, I. Coldicott,G. Hautbergue,C. Webster,L. Castelli,S. Simon,M. Myszczynska,L. Ferraiuolo,M. AzzouzHUMAN GENE THERAPY(2019)引用 0|浏览12暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要