A Phase 2 Clinical Trial Assessing Efficacy And Safety Of The Mtor Inhibitor Sirolimus In The Treatment Of Generalized Lymphatic Anomaly, Kaposiform Lymphangiomatosis, And Gorham-Stout Disease

K. W. Ricci, C. C. Trenor Iii,A. M. Hammill,A. A. Vinks,M. N. Patel, G. Chaudry, M. S. Wentzel, P. S. Mobberley-Schuman,C. Chute, J. Eile,A. Gupta,A. C. Merrow,R. Dasgupta, B. H. Dickie,R. G. Azizkhan, L. Fei,L. Hornung,D. M. Adams

AMERICAN JOURNAL OF RESPIRATORY AND CRITICAL CARE MEDICINE(2015)

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