FINAL RESULTS OF A RANDOMIZED, OPEN-LABEL, MULTICENTER, 26-WEEK DOSE ESCALATION STUDY OF HQK-1001 (2,2-DIMETHYLBUTYRATE, SODIUM SALT) IN SICKLE CELL DISEASE (SCD)
AMERICAN JOURNAL OF HEMATOLOGY(2013)
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AMERICAN JOURNAL OF HEMATOLOGY(2013)