Accepted Manuscript Management strategies for CLN 2 disease
semanticscholar(2017)
摘要
Ruth E. Williams, DM, FRCPCH, Heather R. Adams, PhD, Martin Blohm, MD, Jessica L. Cohen-Pfeffer, MD, Emily de los Reyes, MD, Jonas Denecke, MD, Kristen Drago, RN, CHPPN, Charlie Fairhurst, MBBS, FRCPCH, Margie Frazier, PhD, Norberto Guelbert, MD, PhD, Szilárd Kiss, MD, Annamaria Kofler, PT, John A. Lawson, BMed, FRACP, PhD, Lenora Lehwald, MD, Mary-Anne Leung, SRD, Svetlana Mikhailova, MD, Jonathan W. Mink, MD, PhD, Miriam Nickel, MD, Renée Shediac, PhD, Katherine Sims, MD, Nicola Specchio, MD, PhD, Meral Topcu, MD, Ina von Löbbecke, PT, Andrea West, MSc, Boris Zernikow, MD, PhD, Angela Schulz, MD, PhD
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