Gene therapy PR006 increased progranulin levels and improved lysosomal related phenotypes in model systemsAlissa Brandes,Laura D. Heckman,Li Chin Wong, Zhaohui Yang,Tim Fenn,Stuart Nelson,Zarah Aziz,Sid Kamalakaran,Swetha Garimalla,Suzanne Burstein,Jorge Haller,Jason Politi,Yong Dai,Franz Hefti,Asa AbeliovichMolecular Genetics and Metabolism(2020)引用 0|浏览4暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要