Preclinical development of , an investigational liver-directed AAV gene therapy for the treatment of Pompe diseaseSean M. Armour, Jayme M.L. Nordin,Helena Costa Verdera,Pauline Sellier, George M. Preston, Christopher Riling,Daniel M. Cohen,Fanny Collaud,Marco Crosariol,William J. Quinn,Hayley Hanby,Umut Cagin,Francesco Puzzo,Virginia Haurigot,Giuseppe Ronzitti,Pasqualina Colella,Xavier M. Anguela,Federico MingozziMolecular Genetics and Metabolism(2020)引用 0|浏览14暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要