Intrathecal administration of AVXS-101 gene-replacement therapy (GRT) for spinal muscular atrophy type 2 (SMA2): Phase 1/2A study (strong)R.S. Finkel,J.W. Day,B.T. Darras,N.L. Kuntz,A.M. Connolly,T.O. Crawford,R.J. Butterfield,P.B. Shieh,G. Tennekoon,S.T. Iannaccone, M. Meriggioli, F.G. Ogrinc,S. Kavanagh,E. Kernbauer,J. Whittle,J. L'Italien,B. Kaspar,D.M. Sproule,S.A. Spector,D.E. Feltner,J.R. MendellJOURNAL OF THE NEUROLOGICAL SCIENCES（2019）引用 2|浏览56暂无评分AI 理解论文溯源树样例生成溯源树，研究论文发展脉络Chat Paper正在生成论文摘要
