P.71The emerging phenotype in long-term enzyme-treated classic infantile Pompe patients: severe distal muscle weakness

J. van den Dorpel, E. Poelman, L. Harlaar,H. Kooten, L. van der Giessen,P. van Doorn,A. van der Ploeg,J. van den Hout,N. van der Beek

Neuromuscular Disorders(2019)

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