Envision, A Phase 3 Study To Evaluate Efficacy And Safety Of Givosiran, An Investigational Rnai Therapeutic Targeting Aminolevulinic Acid Synthase 1, In Acute Hepatic Porphyria PatientsManisha Balwani,Laurent Gouya,David Rees,Penelope Stein,Ulrich Stölzel,Paula Aguilera,D Montgomery Bissell,Herbert Bonkovsky,Sioban Keel,Charles Parker,John Phillips,Samuel Silver,Jerzy Windyga,Delia D’avola,Gayle Ross,Peter Stewart,Bruce Ritchie,Jeeyoung Oh,Pauline Harper,Jiaan-Der Wang,Janneke Langendonk,Aneta Ivanova,Yutaka Horie,Karl Anderson,Paolo Ventura,Amy Chan,Craig Penz,Amy Simon,Quinn Dinh,Gary Liu,Eliane SardhJOURNAL OF HEPATOLOGY(2019)引用 8|浏览18暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要