Phase 1/2 Evaluation Of Intrathecal 2-Hydroxypropyl-Beta-Cyclodextrin For The Treatment Of Niemann-Pick Disease Type C1Forbes D. Porter,Nicole Y. Farhat,Elizabeth A. Ottinger,John C. Mckew,Lisa Weissfeld, Ben Machielse,Elizabeth M. Berry-Kavis,Charles H. Vite,Steven U. Walkley,Daniel S. OryMOLECULAR GENETICS AND METABOLISM(2016)引用 4|浏览31暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要