Impact of three decades of improvements in standards of care on clinical outcomes in Duchenne muscular dystrophy

H.J.A. van Ruiten, A.C. Jimenez-Moreno, E. Elliot,A. Mayhew,M. James, C. Marini-Bettolo,Hanns Lochmüller,Volker Straub,K. Bushby,M. Guglieri

European Journal of Paediatric Neurology(2017)

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