Long-term efficacy of enzyme-replacement therapy in 102 adult Pompe patients: a 5-year nationwide prospective cohort study L. Harlaar,Esther Kuperus,Michelle E. Kruijshaar,Stephan C.A. Wens,J. de Vries,Marein M. Favejee,J.C. van der Meijden,Dimitris Rizopoulos,Esther Brusse,P. A. van Doorn,A.T. van der Ploeg,N.A.M. van der BeekNEUROMUSCULAR DISORDERS(2017)引用 0|浏览41暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要