Long-term treatment with eteplirsen promotes exon 51 skipping and novel dystrophin protein production in Duchenne muscular dystrophy patients

J. Charleston, F.J. Schnell,J. Dworzak,C. Donoghue,Sarah Lewis,L. Rodino-Klapac,Zarife Sahenk,C. Shanks,J. Voss, U. DeAlwis,D. Frank, B. Wentworth

NEUROMUSCULAR DISORDERS(2016)

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