Transfusion independence and HMGA2 activation after gene therapy of human [bgr]-thalassaemia
Marina Cavazzana-Calvo,Emmanuel Payen,Salima Hacein-Bey-Abina,Laure Caccavelli,Alain Fischer,Olivier Negre,Floriane Fusil,Leila Maouche-Chrétien,Stany Chrétien,Yves Beuzard,Stany Chrétien,Jean Soulier,Jérôme Larghero,Nabil Kabbara,Bruno Dalle, Bernard Gourmel,Gérard Socie,Yves Beuzard,Eliane Gluckman,Olivier Negre,Beatrix Gillet-Legrand,Gary Wang,Troy Brady,Frederick Bushman,Kathleen Hehir,Julian Down,Maria Denaro,Karen Westerman, Ronald Dorazio, Geert-Jan Mulder,Axel Polack,Resy Cavallesco,Riccardo Sgarra,Françoise Bernaudin,Robert Girot,Arthur Bank,Nathalie Cartier,Patrick Aubourg,Kenneth Cornetta,Frédéric Galacteros NATURE(2010)
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Therapeutics, Cell biology, Medical research
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