P05.4 Brain gene therapy for Metachromatic Leukodystrophy: from bench to bedside C. Sevin,T. Roujeau,F. Piguet,D. Sondhi,M.-A. Colle, S. Raoul,J.-Y. Deschamps, C. Bouquet,M. Vanier, P. Moullier,Y. Cherel,N.R. Hackett,M. Zerah,R.G. Crystal,N. Cartier, P. AubourgEuropean Journal of Paediatric Neurology(2011)引用 24|浏览13暂无评分AI 理解论文溯源树样例生成溯源树,研究论文发展脉络Chat Paper正在生成论文摘要