T REATMENT OF X-L INKED S EVERE C OMBINED I MMUNODEFICIENCY BY IN U TERO T RANSPLANTATION OF P ATERNAL B ONE M ARROW

A LAN W. F LAKE, M ARIA-G RAZIA R ONCAROLO,J ENNIFER, M. P UCK,G RAZA,M ARK I. E VANS,M ARK P. J OHNSON, M. A BELLA, UANE D. H ARRISON,E SMAIL D. Z ANJANI

msra(2010)

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