Results of Prolonged Follow-Up of Late-Onset Pompe Disease Treated with Alglucosidase Alfa (Myozyme®)

NEUROMUSCULAR DISORDERS(2011)

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摘要
Results of Prolonged Follow-Up of Late-Onset Pompe Disease Treated with Alglucosidase Alfa (Myozyme) P. Laforet; C. Payan; K. Laloui; J-Y. Hogrel; C. Wary; R. Carlier; N. Pellegrini; A-L. Bedat-Millet; . Durieu; A. Furby; I. Penisson-Besnier; J. Praline; D. Orlikowski; N. Guffon-Fouilhoux; A. Levy; and B. Eymard Groupe Hospitalier Pitie-Salpetriere, Assistance Publique-Hopitaux de Paris, Centre de reference de pathologie neuromusculaire Paris-Est, Paris; Institut de Myologie, Hopital Pitie-Salpetriere, Paris; CEA, FBM, MIRCen, IdM NMR Laboratory, Paris; Hopital Raymond Poincare, Garches, Assistance Publique-Hopitaux de Paris; Centre hospitalier de de Rouen; Groupe Hospitalier Lyon Sud; Centre hospitalier de St-Etienne; Centre ospitalier d’Angers; Hopital de Tours; Hopital Edouard Herriot-Centre de Reference des Maladies Hereditaires du Metabolisme de Lyon; Centre hospitalier de Rouen, France
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