The risks of therapeutic misconception and individual patient (n=1) “trials” in rare diseases such as Duchenne dystrophy
Annemieke Aartsma-Rus,Pat Furlong,Elizabeth Vroom,Gert-Jan van Ommen,Erik Niks,Chiara Straathof,Jan Verschuuren,Annemieke Aartsma-Rus,Alessandra Ferlini,Lynn Hagger,Emma Heslop,Veronika Karcagi,Jan Kirschner,Pauline McCormack,Pat Moeschen,Francesco Muntoni,Marie-Christine Ouillade,Jes Rahbeck,Christoph Rehmann-Sutter,Francoise Rouault,Tomas Sejersen,Elizabeth Vroom,Simon Woods Neuromuscular Disorders(2011)
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